Publication
Effects of Chronic, Maximal Phosphorodiamidate Morpholino Oligomer (PMO) Dosing on Muscle Function and Dystrophin Restoration in a Mouse Model of Duchenne Muscular Dystrophy
Margaret E. Benny Klimek, Maria Candida Vila, Katie Edwards, Jessica Boehler, James Novak, Aiping Zhang, Jack Van der Meulen, Kathleen Tatum, James Quinn, Alyson Fiorillo, Umar Burki, Volker Straub, Qi Long Lu, Yetrib Hathout, John van Den Anker, Terence A. Partridge, Melissa Morales, Eric Hoffman, Kanneboyina Nagaraju
Journal of Neuromuscular Diseases, November 2021, IOS Press
DOI: 10.3233/jnd-210701