Publication
RNA-LNP–mediated in vivo prime editing corrects disease phenotypes in a mouse model of citrullinemia type I
András Tálas, Eleonora I. Ioannidi, Yanik Weber, Tatjana Haenggi, Péter István Kulcsár, Nadia Zürcher, Erica Faccin, Woohyun J. Moon, Lucas Kissling, Elina Andrea Villiger, Mai Matsushita, Tanja Rothgangl, Sharan Janjuha, Paulo J. C. Lin, Martin Poms, Hiromi Muramatsu, Máté Vadovics, Andreas Reichmuth, Manfred Kopf, Norbert Pardi, Ying K. Tam, Johannes Häberle, Gerald Schwank
Science Translational Medicine, May 2026, American Association for the Advancement of Science
DOI: 10.1126/scitranslmed.aec7274