Publication
Treatment of a severe vascular disease using a bespoke CRISPR–Cas9 base editor in mice
Christiano R. R. Alves, Sabyasachi Das, Vijai Krishnan, Leillani L. Ha, Lauren R. Fox, Hannah E. Stutzman, Claire E. Shamber, Pazhanichamy Kalailingam, Siobhan McCarthy, Christian L. Lino Cardenas, Claire E. Fong, Takahiko Imai, Sunayana Mitra, Shuqi Yun, Rachael K. Wood, Friederike M. C. Benning, Kangsan Roh, Joseph Lawton, Nahye Kim, Rachel A. Silverstein, Joana Ferreira da Silva, Demitri de la Cruz, Rashmi Richa, Jun Xie, Heather L. Gray-Edwards, Rajeev Malhotra, David Y. Chung, Luke H. Chao, Shengdar Q. Tsai, Casey A. Maguire, Mark E. Lindsay, Benjamin P. Kleinstiver, Patricia L. Musolino
Nature Biomedical Engineering, September 2025, Springer Science + Business Media
DOI: 10.1038/s41551-025-01499-1