What is it about?

This is a brief perspective piece that summarizes the key clinical information, the cost-effectiveness analysis, and the policy implications of the research.

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Why is it important?

Patisiran and inotersen are new drugs for a condition that previously have very few effective options. However, high drug prices associated with these drugs prompt questions about cost-effectiveness.

Perspectives

This perspective piece provides a brief summary of a full ICER report and a full day public meeting. One can read the full report and view the webcast of the meeting, but this paper provides a quick summary of all the key elements.

William Dreitlein
Institute for Clinical and Economic Review

Read the Original

This page is a summary of: The Effectiveness and Value of Patisiran and Inotersen for Hereditary Transthyretin Amyloidosis, Journal of Managed Care & Specialty Pharmacy, January 2019, Academy of Managed Care Pharmacy,
DOI: 10.18553/jmcp.2019.25.1.010.
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