Publication
Real‐life experience with inotersen in hereditary transthyretin amyloidosis with late‐onset phenotype: Data from an early‐access program in Italy
Marco Luigetti, Giovanni Antonini, Andrea Di Paolantonio, Luca Gentile, Marina Grandis, Luca Leonardi, Alessandro Lozza, Fiore Manganelli, Anna Mazzeo, Roberta Mussinelli, Filomena My, Laura Obici, Elena Maria Pennisi, Marina Romozzi, Massimo Russo, Mario Sabatelli, Alessandro Salvalaggio, Matteo Tagliapietra, Stefano Tozza
European Journal of Neurology, March 2022, Wiley
DOI: 10.1111/ene.15325