What is it about?

Adult onset Pompe patients are a difficult group to treat a consensus was reached on criteria for ERT

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Why is it important?

ERT is a rather expensive treatment and independent consensus is important


Further therapies can be evaluated by the consortium. This is the first European consensus recommendation for starting and stopping ERT in adult patients with Pompe disease, based on the extensive experience of expert

Prof Corrado Angelini
Universita degli Studi di Padova Polo Bibliotecario di Scienze Farmacologia e Scienze Farmaceutiche

Read the Original

This page is a summary of: European consensus for starting and stopping enzyme replacement therapy in adult patients with Pompe disease: a 10-year experience, European Journal of Neurology, May 2017, Wiley, DOI: 10.1111/ene.13285.
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