What is it about?
Adult onset Pompe patients are a difficult group to treat a consensus was reached on criteria for ERT
Photo by Ben White on Unsplash
Why is it important?
ERT is a rather expensive treatment and independent consensus is important
Read the Original
This page is a summary of: European consensus for starting and stopping enzyme replacement therapy in adult patients with Pompe disease: a 10-year experience, European Journal of Neurology, May 2017, Wiley, DOI: 10.1111/ene.13285.
You can read the full text:
The following have contributed to this page