Publication
Phase 3 Trial of Oral Infigratinib in Children with Achondroplasia
Ravi Savarirayan, Julie Hoover-Fong, Melita Irving, Paul Arundel, Josep Maria de Bergua, Philippe M. Campeau, Toby Candler, Benjamin T. Cocanougher, Valerie Cormier-Daire, Thomas Edouard, Svein O. Fredwall, Paul Harmatz, Daniel Hoernschemeyer, Henrik U. Irgens, Saumya Jamuar, Peter Kannu, Janet M. Legare, Antonio Leiva-Gea, Helen McDevitt, Roberta Onesimo, John Phillips III, Mariana del Pino, Marie-Eve Robinson, Massimiliano Rossi, Mars Skae, Leanne M. Ward, Klane K. White, Jane Schmidt, Ted Lystig, Ariana Salvatici, Yun Bai, Peter W. Butler, David van Veenhuyzen, Daniela Rogoff
The New England Journal of Medicine and Surgery and the Collateral Branches of Science, September 2026, New England Journal of Medicine (NEJM/MMS)
DOI: 10.1056/nejmoa2604565