Publication
Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy
Florian Eichler, Christine Duncan, Patricia L. Musolino, Paul J. Orchard, Satiro De Oliveira, Adrian J. Thrasher, Myriam Armant, Colleen Dansereau, Troy C. Lund, Weston P. Miller, Gerald V. Raymond, Raman Sankar, Ami J. Shah, Caroline Sevin, H. Bobby Gaspar, Paul Gissen, Hernan Amartino, Drago Bratkovic, Nicholas J.C. Smith, Asif M. Paker, Esther Shamir, Tara O’Meara, David Davidson, Patrick Aubourg, David A. Williams
The New England Journal of Medicine and Surgery and the Collateral Branches of Science, October 2017, New England Journal of Medicine (NEJM/MMS)
DOI: 10.1056/nejmoa1700554