Publication
A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase Deficiency
Barbara K. Burton, Manisha Balwani, François Feillet, Ivo Barić, T. Andrew Burrow, Carmen Camarena Grande, Mahmut Coker, Alejandra Consuelo-Sánchez, Patrick Deegan, Maja Di Rocco, Gregory M. Enns, Richard Erbe, Fatih Ezgu, Can Ficicioglu, Katryn N. Furuya, John Kane, Christina Laukaitis, Eugen Mengel, Edward G. Neilan, Scott Nightingale, Heidi Peters, Maurizio Scarpa, K. Otfried Schwab, Vratislav Smolka, Vassili Valayannopoulos, Marnie Wood, Zachary Goodman, Yijun Yang, Stephen Eckert, Sandra Rojas-Caro, Anthony G. Quinn
The New England Journal of Medicine and Surgery and the Collateral Branches of Science, September 2015, New England Journal of Medicine (NEJM/MMS)
DOI: 10.1056/nejmoa1501365