Publication
A Modified γ-Retrovirus Vector for X-Linked Severe Combined Immunodeficiency
Salima Hacein-Bey-Abina, Sung-Yun Pai, H. Bobby Gaspar, Myriam Armant, Charles C. Berry, Stephane Blanche, Jack Bleesing, Johanna Blondeau, Helen de Boer, Karen F. Buckland, Laure Caccavelli, Guilhem Cros, Satiro De Oliveira, Karen S. Fernández, Dongjing Guo, Chad E. Harris, Gregory Hopkins, Leslie E. Lehmann, Annick Lim, Wendy B. London, Johannes C.M. van der Loo, Nirav Malani, Frances Male, Punam Malik, M. Angélica Marinovic, Anne-Marie McNicol, Despina Moshous, Benedicte Neven, Matías Oleastro, Capucine Picard, Jerome Ritz, Christine Rivat, Axel Schambach, Kit L. Shaw, Eric A. Sherman, Leslie E. Silberstein, Emmanuelle Six, Fabien Touzot, Alla Tsytsykova, Jinhua Xu-Bayford, Christopher Baum, Frederic D. Bushman, Alain Fischer, Donald B. Kohn, Alexandra H. Filipovich, Luigi D. Notarangelo, Marina Cavazzana, David A. Williams, Adrian J. Thrasher
The New England Journal of Medicine and Surgery and the Collateral Branches of Science, October 2014, New England Journal of Medicine (NEJM/MMS)
DOI: 10.1056/nejmoa1404588