Publication
A Phase 3 Trial of Vosoritide in Children with Hypochondroplasia
Andrew Dauber, Ravi Savarirayan, Philippe M. Campeau, Ricki S. Carroll, Moira Cheung, Valérie Cormier-Daire, Josep Maria de Bergua, Thomas Edouard, Michaela Veronika Gonfiantini, Julie Hoover-Fong, Peter Kannu, Yutaka Kinoshita, Takuo Kubota, Roberto Mendoza-Londono, Noriyuki Namba, Yasuhisa Ohata, Roberta Onesimo, Katja Palm, Carlos E. Prada, Rachel Reynaud, Massimiliano Rossi, Oliver Semler, Kei Takasawa, Roberto Bassi, Sajda Ghani, Alice Huntsman Labed, Dane Osmond, Ian Sabir, Jeanette White, Mohamad Maghnie
NEJM Evidence, September 2026, New England Journal of Medicine (NEJM/MMS)
DOI: 10.1056/evidoa2600257