Publication
Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia
Paula Río, Susana Navarro, Wei Wang, Rebeca Sánchez-Domínguez, Roser M. Pujol, José C. Segovia, Massimo Bogliolo, Eva Merino, Ning Wu, Rocío Salgado, María L. Lamana, Rosa M. Yañez, José A. Casado, Yari Giménez, Francisco J. Román-Rodríguez, Lara Álvarez, Omaira Alberquilla, Anna Raimbault, Guillermo Guenechea, M. Luz Lozano, Laura Cerrato, Miriam Hernando, Eva Gálvez, Raquel Hladun, Irina Giralt, Jordi Barquinero, Anne Galy, Nagore García de Andoín, Ricardo López, Albert Catalá, Jonathan D. Schwartz, Jordi Surrallés, Jean Soulier, Manfred Schmidt, Cristina Díaz de Heredia, Julián Sevilla, Juan A. Bueren
Nature Medicine, September 2019, Springer Science + Business Media
DOI: 10.1038/s41591-019-0550-z