Publication
Elivaldogene Autotemcel (eli-cel, Lenti-D) Gene Therapy for the Treatment of Cerebral Adrenoleukodystrophy: Updated Results from the Phase 2/3 ALD-102 Study and First Report on Safety Outcomes from the Phase 3 ALD-104 Study
Paul J. Orchard, Christine N. Duncan, Florian S. Eichler, Satiro N. De Oliveira, Adrian J. Thrasher, Caroline Sevin, Hernan M. Amartino, Nicholas J.C. Smith, Jörn-Sven Kühl, Daniel Kenney-Jung, Robert Chiesa, Jean-Hugues Dalle, Jing Xu, Andrew C. Dietz, Elizabeth McNeil, Patrick Aubourg, David A. Williams
Transplantation and Cellular Therapy, March 2021, Elsevier
DOI: 10.1016/s2666-6367(21)00149-4