Publication
30. Phase II Clinical Trial of Gene Therapy for Adenosine Deaminase-Deficient Severe Combined Immune Deficiency (ADA-SCID) Using a γ-Retroviral Vector
Kit L. Shaw, Elizabeth Garabedian, Rob Sokolic, Provaboti Barman, Alejandra Davila, Christopher Silvin, Satiro de Oliveira, Ami J. Shah, Dayna Terrazas, Denise Carbonaro, Sabine Geiger, Suparna Mishra, Aaron Cooper, Monika Smogorzewska, Jayashree Jagadeesh, Michael S. Hershfield, Alan Wayne, Gay M. Crooks, Theodore Moore, Fabio Candotti, Donald B. Kohn
Molecular Therapy, May 2015, Elsevier
DOI: 10.1016/s1525-0016(16)33634-6