Publication
Safety and efficacy of deferiprone for pantothenate kinase-associated neurodegeneration: a randomised, double-blind, controlled trial and an open-label extension study
Thomas Klopstock, Fernando Tricta, Lynne Neumayr, Ivan Karin, Giovanna Zorzi, Caroline Fradette, Tomasz Kmieć, Boriana Büchner, Hannah E Steele, Rita Horvath, Patrick F Chinnery, Anna Basu, Clemens Küpper, Christiane Neuhofer, Bernadette Kálmán, Petr Dušek, Zuhal Yapici, Ian Wilson, Feng Zhao, Federica Zibordi, Nardo Nardocci, Christine Aguilar, Susan J Hayflick, Michael Spino, Andrew M Blamire, Penelope Hogarth, Elliott Vichinsky
The Lancet Neurology, July 2019, Elsevier
DOI: 10.1016/s1474-4422(19)30142-5