Publication
Preclinical quality, safety, and efficacy of a CGMP iPSC-derived myogenic progenitor product for the treatment of muscular dystrophies
Karim Azzag, Alessandro Magli, James Kiley, Darin Sumstad, Diane Kadidlo, Sarah B. Crist, Beverly Norris, Aaron Ahlquist, Laura L. Hocum Stone, John Everett, Jill Shappa Faustich, Davis Seelig, Parthasarathy Rangarajan, Hyunkee Kim, Craig Flory, Frederic Bushman, Sabarinathan Ramachandran, Peter B. Kang, Robert J. Schumacher, John E. Wagner, Michael Kyba, Melanie L. Graham, David H. McKenna, Rita C.R. Perlingeiro
Molecular Therapy, October 2025, Elsevier
DOI: 10.1016/j.ymthe.2025.07.007