Publication
Development of a core outcome set for mucopolysaccharidoses (MPS) in children: Results from Delphi surveys and a consensus workshop
Alison H. Howie, Alexandra Wyatt, Michal Inbar-Feigenberg, John J. Mitchell, Maureen Smith, Kim Angel, Jenifer Gentle, Nancy J. Butcher, Martin Offringa, Philippe M. Campeau, Alicia K. Chan, Pranesh Chakraborty, Andrea Chow, Farah El Turk, Cheryl R. Greenberg, Eva Mamak, Aziz Mhanni, Tony Rupar, Rebecca Sparkes, Kednapa Thavorn, Kylie Tingley, Beth K. Potter
Molecular Genetics and Metabolism, February 2023, Elsevier
DOI: 10.1016/j.ymgme.2022.107154