Publication
P001: Lower extremity alignment improvements correlate with physical functioning in children with achondroplasia treated with navepegritide: 52-week ApproaCH trial results*
Janet Legare, Leanne Ward, Daniel Hoernschemeyer, Hanne Hove, Carlos Bacino, Philippe Campeau, Paul Hofman, Josep Maria de Bergua Domingo, M. Jennifer Abuzzahab, Kevin Smit, Sasha Carsen, Andrew Tice, Stefan Jackowski, Maya Scharke, Meng Mao, Lærke Clement Freiberg, Michael Makara, Michael Ominsky, Aimee Shu, Ravi Savarirayan, Ciara McDonnell
Genetics in Medicine Open, January 2026, Elsevier
DOI: 10.1016/j.gimo.2026.103492