Publication
Safety of Autologous Hematopoietic Stem Cell Transplantation with Gene Addition Therapy for Transfusion-Dependent β-Thalassemia, Sickle Cell Disease, and Cerebral Adrenoleukodystrophy
Mark C. Walters, Franco Locatelli, Adrian J. Thrasher, John F. Tisdale, Paul J. Orchard, Christine N. Duncan, Jörn-Sven Kühl, Satiro Nakamura De Oliveira, Martin G. Sauer, Andreas E. Kulozik, Evangelia Yannaki, Suradej Hongeng, Markus Y. Mapara, Lakshmanan Krishnamurti, Olivier Hermine, Stephane Blanche, Patrick Aubourg, Nicholas J.C. Smith, Weiliang Shi, Richard A. Colvin, Elizabeth McNeil, Jean-Antoine Ribeil, Marina Cavazzana, David A. Williams
Biology of Blood and Marrow Transplantation, March 2020, Elsevier
DOI: 10.1016/j.bbmt.2019.12.104