Publication
Lenti-D Hematopoietic Stem Cell Gene Therapy to Arrest Progression of Cerebral Adrenoleukodystrophy: Interim Results of an International Phase 2/3 Trial
Christine Duncan, Florian Eichler, Patricia L. Musolino, Paul J. Orchard, Satiro De Oliveira, Adrian J. Thrasher, Myriam A. Armant, Colleen Dansereau, Troy C. Lund, Weston P. Miller, Gerald V. Raymond, Raman Sankar, Ami J. Shah, Caroline Sevin, H. Bobby Gaspar, Paul Gissen, Hernan Amartino, Drago Bratkovic, Nicholas J.C. Smith, Asif M. Paker, Esther Shamir, Tara O'Meara, Mohammed Asmal, David Davidson, Patrick Aubourg, David A. Williams
Biology of Blood and Marrow Transplantation, March 2018, Elsevier
DOI: 10.1016/j.bbmt.2017.12.642