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  1. The Impact of Fabry Disease on Reproductive Fitness
  2. Detection of three families with GLA p.A143T mutation and low α-galactosidase levels by newborn screening for Fabry disease
  3. PRX-102 for treating Fabry disease: immunogenicity and PK results from a phase 1-2 study
  4. One-year follow up of Fabry disease patients treated by IV administration of a plant derived alpha-Gal-A enzyme: safety and efficacy
  5. The impact of Fabry disease on reproductive fitness
  6. Novel treatment for Fabry disease: IV administration of plant derived alpha-gal-A enzyme safety and efficacy interim report
  7. Oral Migalastat HCl Leads to Greater Systemic Exposure and Tissue Levels of Active α-Galactosidase A in Fabry Patients when Co-Administered with Infused Agalsidase
  8. Recommendation for initiation and cessation of enzyme replacement therapy
  9. Comparison of clinical practice guidelines and actual clinical practice in Fabry disease diagnosis
  10. A phase 2a study to investigate the effect of a single dose of migalastat HCl, a pharmacological chaperone, on agalsidase activity in subjects with Fabry disease
  11. Transplantation - clinical I
  12. 45. Myocardial infiltration in Anderson–Fabry disease: A case report
  13. Effect of in vivo lymphocyte-depleting strategies on development of lymphoproliferative disorders in children post allogeneic bone marrow transplantation
  14. Successful allogeneic hematopoietic stem cell transplantation (HSCT) for Shwachman–Diamond syndrome
  15. Epstein Barr virus associated lymphoproliferative disease following T-cell depleted pediatric bone marrow transplantation, retrospective analysis of potential risk factors at a single institute
  16. Poor outcome in children with refractory/relapsed leukemia undergoing bone marrow transplantation with mismatched family member donors
  17. Ten‐year experience of unrelated bone marrow donor transplants in children with malignant and non‐malignant conditions
  18. #679 Bone marrow transplantation using mismatched, Dr-identical, or matched family member donors for children with refractory or relapsed leukemia
  19. Complete heart block in association with graft-versus-host disease
  20. Successful program to prevent aspergillus infections in children undergoing marrow transplantation: use of nasal amphotericin
  21. Bone Marrow Transplantation Improves Survival for Acute Lymphoblastic Leukemia in Relapse: A Preliminary Report
  22. INFECTIOUS COMPLICATIONS FOLLOWING MISMATCHED VERSUS MATCHED ALLOGENEIC BONE MARROW TRANSPLANTATION (BMT)
  23. 23. IMPROVED SURVIVAL IN RELAPSED ACUTE LYMPHOBLASTIC LEUKEMIA WITH BONE MARROW TRANSPLANTATION
  24. Prostaglandin E1 Bladder Instillations to Control Severe Hemorrhagic Cystitis
  25. Effects of acute atrial fibrillation on the vasodilator reserve of the canine atrium
  26. Quantitative angiographic morphology of coronary stenoses leading to myocardial infarction or unstable angina
  27. Transluminal, subselective measurement of coronary artery blood flow velocity and vasodilator reserve in man